Pharmacologically controlled vector for CNS gene therapies

Written by Martin Groß on 21 January 2020.

Regulatable CNS gene therapy reduces side effects

Gene therapies are irreversible and not controlable in case of side effects. We offer a pharmacologically controlled one-vector expression system of a therapeutic factor (i.e. GDNF) with zero background expression, based on mifepristone (Mfp)-Gene Switch system, for the therapy of neurological diseases.